Burosumab treatment in adults with X-linked hypophosphataemia: 96-week patient-reported outcomes and ambulatory function from a randomised phase 3 trial and open-label extension.
Karine BriotAnthony A PortaleMaria Luisa BrandiThomas O CarpenterHae Ii CheongMartine Cohen SolalRachel K CrowleyRichard EastellYasuo ImanishiSteven IngKarl InsognaNobuaki ItoSuzanne Jan de BeurMuhammad K JavaidPeter KamenickyRichard KeenTakuo KubotaRobin H LachmannFarzana PerwadPisit PitukcheewanontStuart H RalstonYasuhiro TakeuchiHiroyuki TanakaThomas J WeberHan-Wook YooAnnabel NixonMark NixonWei SunAngela WilliamsErik Allen ImelPublished in: RMD open (2021)
NCT02526160.