Outcomes for studies assessing the efficacy of hemostatic therapies in persons with congenital bleeding disorders.
Camila Catherine AquinoVictoria Borg DebonoFederico GerminiDrashti PeteChristine L KemptonGuy Aaron YoungRobert SidonioStacy E CroteauAmy L DunnNigel S KeyAlfonso IorioPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2021)
Primary outcomes for clinical trials assessing the efficacy of hemostatic treatment in achieving control, prevention and limiting long-term consequences of bleeding in inherited bleeding disorders are suggested, and their strength and limitations discussed.