Who should be eligible for gene therapy clinical trials in red blood cell pyruvate kinase deficiency (PKD)?: Toward an expanded definition of severe PKD.
Jonathan D SchwartzWilma BarcelliniRachael F F GracePaola BianchiAlberto ZanellaJosé Luis López LorenzoJulian SevillaAmi J ShahBertil GladerEileen NicolettiSusana Navarro OrdoñezJosé Carlos SegoviaPublished in: American journal of hematology (2022)