Home-based gait analysis as an exploratory endpoint during a multicenter phase 1 trial in limb girdle muscular dystrophy type R2 and facioscapulohumeral muscular dystrophy.
Teresa GidaroErwan GasnierMelanie AnnoussamyJohn VissingShahram AttarianTahseen MozaffarStanley IyaduraiKathryn R WagnerDavid VissièreGennyne WalkerSanjay S ShuklaLaurent ServaisPublished in: Muscle & nerve (2021)
The present study suggests that home-recorded stride speed constitutes a precise and sensitive outcome in ambulant patients with FSHD and LGMDR2.