A Systematic Review and Meta-analyses of Longitudinal Studies on Drug Treatments for Gaucher Disease.

Letícia Paula LeonartMariana M FachiBeatriz BögerMariana Ribeiro da SilvaRenata SzpakNatália Fracaro LombardiMaria Lucia Alves PedrosoRoberto Pontarolo

Published in: The Annals of pharmacotherapy (2022)

The results were favorable for all ERTs and for eliglustat. Based on the assessed evidence, miglustat did not achieved expressive results. However, all evidence should be interpreted considering its limitations and does not replace well-conducted randomized trials.

Keyphrases

meta analyses
systematic review
randomized controlled trial
emergency department
replacement therapy
adverse drug