MiRNA Expression in Patients with Gaucher Disease Treated with Enzyme Replacement Therapy.

Lukasz PawlinskiAnna PolusEwa TobórMaria SordylMarianna KopkaBogdan SolnicaBeata Kiec-Wilk

Published in: Life (Basel, Switzerland) (2020)

We revealed few miRNAs, like miR-26-5p, which are highly altered and fit the GD pathophysiological model, might be considered as novel biomarkers of disease progression but need further evaluation.

Keyphrases

replacement therapy
smoking cessation
poor prognosis
single cell
binding protein
newly diagnosed