Development of a novel PRO instrument for use in familial chylomicronemia syndrome.

David DavidsonChristina SlotaMontserrat Vera-LlonchT Michelle BrownAndrew HsiehSheri E Fehnel

Published in: Journal of patient-reported outcomes (2021)

The content validity of the final 17-item FCS Symptoms and Impacts Scale is strongly supported by patient input gathered through both a large burden-of-illness study and qualitative research. To further support use in clinical trials, psychometric evaluation of the measure is underway.

Keyphrases

clinical trial
case report
systematic review
early onset
randomized controlled trial
anti inflammatory
sleep quality
physical activity
study protocol