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Long-term safety and influence on growth in patients receiving sirolimus: a pooled analysis.

Yang-Yang WangLi-Ping ZouKai-Feng XuWen-Shuai XuMeng-Na ZhangQian LuXin-Lun TianLing-Yu PangWen HeQiu-Hong WangYang GaoLi-Ying LiuXiao-Qiao ChenShu-Fang MaHui-Min ChenShuo DunXiao-Yan YangXiao-Mei LuoLu-Lu HuangYu-Fen Li
Published in: Orphanet journal of rare diseases (2024)
Pediatric patients: Chinese clinical trial registry, No. ChiCTR-OOB-15,006,535. Adult patients: ClinicalTrials, No. NCT03193892.
Keyphrases
  • clinical trial
  • phase ii
  • double blind
  • study protocol
  • randomized controlled trial
  • phase iii