Cross-Sectional Quantitative Evaluation of a Novel Patient-Reported Outcome Measure in Familial Chylomicronemia Syndrome.

T Michelle BrownMontserrat Vera-LlonchChisom KanuAsia Sikora Kessler Aaron Yarlas Sheri E Fehnel

Published in: Patient related outcome measures (2024)

The results of this study support the structure, reliability, and validity of the FCS-SIS, laying the psychometric groundwork for longitudinal evaluation of its utility in assessing treatment benefit in FCS clinical studies.

Keyphrases

cross sectional
patient reported outcomes
high resolution
early onset
case report
combination therapy
replacement therapy
smoking cessation