Effect of Nusinersen in a late onset spinal muscular atrophy patient for 14 months: A case report.
Jin-Mo ParkYu-Sun MinDonghwi ParkJin-Sung ParkPublished in: Medicine (2021)
Although there is limited data on the effect of Nusinersen in late onset SMA patients, our case adds on the effectiveness even in late onset SMA. More studies are needed to consolidate the effects and adverse events of Nusinersen in late onset SMA.