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Elevated methylation levels, reduced expression levels, and frequent contractions in a clinical cohort of C9orf72 expansion carriers.

Jazmyne L JacksonNiCole A FinchMatthew C BakerJennifer M KachergusMariely DeJesus-HernandezKimberly PereiraElizabeth ChristopherMercedes PrudencioMichael G HeckmanE Aubrey ThompsonDennis W DicksonJaimin ShahBjörn OskarssonLeonard PetrucelliRosa RademakersMarka van Blitterswijk
Published in: Molecular neurodegeneration (2020)
In blood from C9orf72 expansion carriers, we found elevated methylation levels, reduced expression levels, and unstable expansions that tend to contract in successive generations, arguing against anticipation.
Keyphrases
  • poor prognosis
  • genome wide
  • binding protein
  • gene expression
  • long non coding rna