Real World Evidence on the Effectiveness of Nusinersen within the National Program to Treat Spinal Muscular Atrophy in Poland.

Dominika KrupaMarcin CzechEwa ChudzyńskaBeata Koń Maria Jędrzejowska

Published in: Healthcare (Basel, Switzerland) (2023)

The drug program to treat SMA improved patient care in Poland. The NHF database was a reliable source to monitor resource-intensive therapies' costs, demography, and selected patient outcomes.

Keyphrases

quality improvement
randomized controlled trial
adverse drug
systematic review
emergency department