Evidence of hydroxyurea activity in children with pretreated desmoid-type fibromatosis: A new option in the armamentarium of systemic therapies.
Andrea C FerrariDaniel OrbachMaria Carmen AffinitaStefano ChiaravalliNadege CorradiniCristina MeazzaGianni BisognoMichela CasanovaPublished in: Pediatric blood & cancer (2018)
This is the first published series on the efficacy of hydroxyurea in pediatric DF. The response rate was moderate, but similar to that reported for other medical therapies currently considered as treatment options in this disease. Though further, larger series are needed to confirm as much, hydroxyurea has potential as an effective alternative therapy for DF.