Diazoxide choline extended-release tablet in people with Prader-Willi syndrome: results from long-term open-label study.
Jennifer L MillerEvelien GeversNicola BridgesJack A YanovskiParisa SalehiKathryn S ObrynbaEric I FelnerLynne M BirdAshley H ShoemakerMoris AnguloMerlin G ButlerDavid StevensonAnthony P GoldstoneJohn WildingMelissa LahM Guftar ShaikhElizabeth LittlejohnM Jennifer AbuzzahabAmy FleischmanPatricia HiranoKristen YenNeil M CowenAnish Bhatnagarnull nullPublished in: Obesity (Silver Spring, Md.) (2023)
DCCR administration to people with PWS was well-tolerated and associated with broad-ranging improvements in the syndrome. Sustained administration of DCCR has the potential to reduce disease severity and the burden of care for families.