A Discrete Choice Experiment to Derive Health Utilities for Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency in France.
Adam B SmithAndria HanburyJennifer A WhittyIgor Beitia Ortiz de ZarateFlorence HammesGérard de PouvourvilleKatharina BueschPublished in: Patient related outcome measures (2022)
A DCE was used to derive health utilities for AADC deficiency. These health utilities will subsequently be used in an economic model evaluating an AADC deficiency intervention.