Eliciting health state utilities for Aromatic L-amino Acid Decarboxylase (AADC) deficiency: a UK vignette study.
Adam B SmithAndria HanburyKatharina BueschPublished in: Journal of patient-reported outcomes (2021)
Health state utilities were derived for AADC deficiency through a vignette study. These will be used for a cost-effectiveness model of an AADC deficiency treatment.