Long-term follow-up in an open-label trial of triheptanoin in GLUT1 deficiency syndrome: a sustained dramatic effect.

Elodie HainqueDomitille GrasAurélie MeneretMariana AtencioMarie-Pierre LutonMagali BarbierMohamed DoulazmiFlorence HabarouChris OttolenghiEmmanuel RozeFanny Mochel

Published in: Journal of neurology, neurosurgery, and psychiatry (2019)

Keyphrases

study protocol
clinical trial
phase iii
phase ii
randomized controlled trial
open label