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Decreased dystrophin expression and elevated dystrophin-targeting miRNAs in anti-HMGCR immune-mediated necrotizing myopathy.

Maude B MarmenZakaria OrfiJunio DortJean-Philippe Proulx-GauthierNicolas ChrestianNicolas A DumontBenjamin Ellezam
Published in: Acta neuropathologica (2023)
Keyphrases
  • muscular dystrophy
  • duchenne muscular dystrophy
  • poor prognosis
  • cancer therapy
  • late onset
  • binding protein
  • long non coding rna
  • drug delivery