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The "Editors" Take to RAG: Promise of CRISPR/Cas9/rAAV6-Based Gene Therapy for RAG2 Deficiency.
Vivien Béziat
Isabelle Meyts
Published in:
Journal of clinical immunology (2021)
Keyphrases
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crispr cas
genome editing
copy number
genome wide
big data
genome wide identification
replacement therapy
transcription factor
artificial intelligence