Effectiveness of Nusinersen in Adolescents and Adults with Spinal Muscular Atrophy: Systematic Review and Meta-analysis.

Tim HagenackerLorenzo MaggiGiorgia CorattiBora YounStephanie RaynaudAngela D ParadisEugenio Mercuri

Published in: Neurology and therapy (2024)

Findings provide consolidated evidence that nusinersen is effective in improving or stabilizing motor function in many adolescents and adults with a broad spectrum of SMA.

Keyphrases

young adults
physical activity
randomized controlled trial
systematic review