Head-to-head trial of pegunigalsidase alfa versus agalsidase beta in patients with Fabry disease and deteriorating renal function: results from the 2-year randomised phase III BALANCE study.
Eric L WallaceOzlem Goker-AlpanWilliam R WilcoxMyrl HolidaJohn BernatNicola LongoAleš LinhartDerralynn A HughesRobert J HopkinCamilla TøndelMirjam LangeveldPilar GiraldoAntonio PisaniDominique Paul GermainAnkit MehtaPatrick B DeeganMaria Judit MolnarDamara OrtizAna JovanovicMichael MurielloBruce A BarshopVirginia KimonisBojan VujkovacAlbina NowakTarekegn GeberhiwotIlkka KantolaJasmine KnollStephen WaldekKhan NeddAmel KaraaEinat Brill-AlmonSari AlonRaul ChertkoffRossana RoccoAnat SakovDavid G WarnockPublished in: Journal of medical genetics (2023)
NCT02795676.