Health-related quality of life in paediatric haemophilia B patients treated with rIX-FP.
Sylvia von MackensenJinesh ShahWilfried SeifertGili KenetPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2018)
Prophylaxis with rIX-FP led to substantial improvements in HRQoL in paediatric patients and treatment satisfaction in caregivers.