Producing a preference-based quality of life measure for people with Duchenne muscular dystrophy: a mixed-methods study protocol.
Philip A PowellJill CarltonDonna RowenJohn E BrazierPublished in: BMJ open (2019)
This study has received ethical approval from the National Health Service (REC reference: 18/SW/0055). The primary output of this research will be a condition-specific PBM (or 'bolt-on' to an existing generic PBM) in people with DMD and an associated value set. Results will be disseminated through international conferences and open-access journals.