An expanded access protocol of RT001 in amyotrophic lateral sclerosis-Initial experience with a lipid peroxidation inhibitor.
Megan YertonAllison WinterAnthony KostovCassandra LiebermanDario GelevskiHarli WeberMichael DoyleGeli KaneNeil ParikhKatherine M BurkeMargot RohrerTaylor StirratMargaret BrunoAlison HochmanSarah LuppinoJennifer ScaliaDebra SkonieckiDerek D'AgostinoErvin SinaniHong YuAlexander V ShermanSuma BabuJames D BerryMark G MideiPeter G MilnerMerit E CudkowiczSabrina PaganoniPublished in: Muscle & nerve (2022)
RT001 was administered safely to a small group of people living with ALS in the context of an EA protocol. Currently, there is an ongoing randomized, double-blind, controlled study of RT001 in ALS.