Real-world use of emicizumab in patients with haemophilia A: Bleeding outcomes and surgical procedures.
Isabella McCaryChristine J GuelcherJanice KuhnRegina ButlerGita MasseyMichael F GuerreraLance BallesterLeslie RaffiniPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2020)
Our favourable clinical experience with emicizumab is similar to that reported in the clinical trials. Notably, this is the largest cohort of patients <12 years without inhibitors treated with emicizumab.