The Two Substrate Reduction Therapies for Type 1 Gaucher Disease Are Not Equivalent. Comment on Hughes et al. Switching between Enzyme Replacement Therapies and Substrate Reduction Therapies in Patients with Gaucher Disease: Data from the Gaucher Outcome Survey (GOS). J. Clin. Med. 2022, 11 , 5158.
Pramod K MistryPriya S KishnaniManisha BalwaniJoel M CharrowJudy HullNeal J WeinrebTimothy M CoxPublished in: Journal of clinical medicine (2023)
In their paper, Hughes et al. [...].