Sickle cell and silent spleen.

Published in: Blood (2015)

In this issue of Blood, in a first-rate example of collaboration between academia (University of California) and industry (Sangamo), Hoban et al show in situ gene correction of sickle cell anemia (SCA), a prototypical hemoglobinopathy.

Keyphrases

genome wide
copy number
iron deficiency
genome wide identification
gene expression
dna methylation