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MERTK missense variants in three patients with retinitis pigmentosa.

Federica E PoliImran H YusufPenny CloustonMorag ShanksJennifer WhitfieldPeter Charbel IssaRobert E MacLaren
Published in: Ophthalmic genetics (2022)
is a promising candidate for viral-mediated gene replacement therapy. Moreover, one variant represents a single nucleotide transition, which is theoretically targetable with CRISPR-Cas9 base-editing.
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