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Profiling the Biochemical Signature of GBA-Related Parkinson's Disease in Peripheral Blood Mononuclear Cells.

Micol AvenaliSilvia CerriGerardo OngariCristina GhezziClaudio PacchettiCristina TassorelliEnza Maria ValenteFabio Blandini
Published in: Movement disorders : official journal of the Movement Disorder Society (2021)
We propose peripheral blood mononuclear cells as an easily accessible and manageable model to provide a distinctive biochemical profile of GBA-PD, potentially useful for patient stratification or selection in clinical trials. © 2021 The Authors. Movement Disorders published by Wiley Periodicals LLC on behalf of International Parkinson and Movement Disorder Society.
Keyphrases
  • clinical trial
  • case report
  • single cell
  • randomized controlled trial
  • systematic review
  • phase ii
  • open label
  • phase iii
  • meta analyses