Development of the Hypertrophic Cardiomyopathy Symptom Questionnaire (HCMSQ): A New Patient-Reported Outcome (PRO) Instrument.
Matthew ReaneyVeleka AllenAmy J SehnertLiang FangAlbert A HagègeSrihari S NaiduIacopo OlivottoPublished in: PharmacoEconomics - open (2022)
Our findings support the HCMSQv1.0 as a fit-for-purpose PRO instrument for assessing treatment benefit in patients with HCM. Studies in larger patient populations are ongoing to confirm responder definition and scoring approaches encompassing key HCM symptoms.