Adoption of emicizumab (Hemlibra®) for hemophilia A in Europe: Data from the 2020 European Association for Haemophilia and Allied Disorders survey.
Evelien KrumbKarin FijnvandraatMichael P MakrisFlora PeyvandiAislin RyanAngelos AthanasopoulosCedric HermansPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2021)
Three years after its rollout in Europe, emicizumab is widely available. Clinical efficacy and safety were evaluated to be very good, keeping in mind the inherent limitations of the study. Unmet needs include establishment of treatment guidelines for surgery and breakthrough bleeding, limited expertise, especially in young children, and availability of laboratory assays.