Tafamidis concentration required for transthyretin stabilisation in cerebrospinal fluid.
Felix J TsaiMarcus JaegerTeresa CoelhoEvan T PowersJeffrey W KellyPublished in: Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis (2023)
Tafamidis stabilises TTR in CSF to what is likely a clinically meaningful extent at CSF concentrations achieved by the normal tafamidis dosing regimen.
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