The Patient Experience of Gene Therapy for Hemophilia: Qualitative Interviews with Trial Patients.

Published in: Patient preference and adherence (2020)

Gene therapy has the potential to change the life of patients with haemophilia not only by the reduction of bleeding events but also by the increase of active and sportive activities.

Keyphrases

gene therapy
end stage renal disease
ejection fraction
chronic kidney disease
prognostic factors
randomized controlled trial
study protocol
phase iii
human health
patient reported
double blind