Investigating Late-Onset Pompe Prevalence in Neuromuscular Medicine Academic Practices: The IPaNeMA Study.

Marie WencelAziz ShaibaniNamita A GoyalMazen M DimachkieJaya TrivediNicholas E JohnsonLaurie GutmannMatthew P WicklundSankar BandyopadhayAngela L GengeMiriam L FreimerNeelam GoyalAlan PestronkJulaine FlorenceChafic KaramJeffrey W RalphZinah RasheedMelissa HaysSteve HopkinsTahseen Mozaffar

Published in: Neurology. Genetics (2021)

Clinical trial registration number: NCT02838368.

Keyphrases

late onset
early onset
clinical trial
primary care
healthcare
risk factors
study protocol
randomized controlled trial
phase ii
double blind