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Treatment of autosomal recessive hearing loss via in vivo CRISPR/Cas9-mediated optimized homology-directed repair in mice.

Xi GuXinde HuDaqi WangZhijiao XuFang WangDi LiGeng-Lin LiHui YangHuawei LiErwei ZuoYilai Shu
Published in: Cell research (2022)
Keyphrases
  • crispr cas
  • hearing loss
  • genome editing
  • high fat diet induced
  • type diabetes
  • metabolic syndrome
  • skeletal muscle
  • autism spectrum disorder