Qualitative Study of the Patient Experience with Venglustat for Gaucher Disease Type 3 in a Phase 2 Open-Label, Multicenter, Multinational Study (LEAP).
Raphael SchiffmannKarl Eugen MengelMary WallaceCamille RochmannJames TurnbullRobert KrupnickChad GwaltneyRuth Pulikottil-JacobIsabela BatsuRiliang ZhengAlaa HamedPublished in: Advances in therapy (2024)
ClinicalTrials.gov identifier, NCT02843035.