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Assessing Preferences for Rare Disease Treatment: Qualitative Development of the Paroxysmal Nocturnal Hemoglobinuria Patient Preference Questionnaire (PNH-PPQ©).

Karen KaiserSusan E YountChrista E MartensKimberly A WebsterSara ShaunfieldAmy SparlingJohn Devin PeipertDavid CellaScott T RottinghausBonnie M K DonatoRichard WellsIoannis Tomazos
Published in: Patient preference and adherence (2020)
The PNH-PPQ provides a patient-centered approach for evaluating preferences for the treatment of PNH. The PNH-PPQ has subsequently assessed patient preference in the clinical trial sub-study ALXN1210-PNH-302s.
Keyphrases
  • clinical trial
  • case report
  • systematic review
  • atrial fibrillation
  • blood pressure
  • randomized controlled trial
  • decision making
  • open label
  • phase iii
  • phase ii