Therapeutic decisions under uncertainty for spinal muscular atrophy: The DECISIONS-SMA study protocol.

Gustavo SaposnikPaola Díaz-AbósVictoria Sánchez-MenéndezCarmen ÁlvarezMaría TerzaghiJorge MaurinoMaría Brañas-PampillónIgnacio Málaga

Published in: PloS one (2022)

The study findings will contribute to better understand relevant factors associated with therapeutic decisions of pediatric neurologists in spinal muscular atrophy, identifying treatment preferences and evaluating the role of behavioral aspects such as therapeutic inertia, herding, regret, and workplace burnout.

Keyphrases

study protocol
randomized controlled trial
clinical trial
open label
smoking cessation
placebo controlled