Valoctocogene Roxaparvovec and Etranacogene Dezaparavovec: Novel Gene Therapies for Hemophilia A and B.

Published in: The Annals of pharmacotherapy (2023)

Valoctocogene and etranacogene provide another treatment for selected patients with hemophilia. Treatment for the patient with hemophilia (gene therapy vs replacement strategy) must be personalized as new clinical data are published being cognizant of drug affordability.

Keyphrases

gene therapy
randomized controlled trial
gene expression
genome wide
case report
dna methylation
combination therapy
replacement therapy
data analysis
genome wide identification