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Response by Li and Chang Regarding Article, "Therapeutic Exon Skipping Through a CRISPR-Guided Cytidine Deaminase Rescues Dystrophic Cardiomyopathy In Vivo".

Jia LiXing Chang
Published in: Circulation (2022)
Keyphrases
  • crispr cas
  • genome editing
  • genome wide
  • heart failure
  • mouse model
  • ion batteries
  • gene expression