Improved therapeutic approach for spinal muscular atrophy via ubiquitination-resistant survival motor neuron variant.
Joonwoo RheeJong-Seol KangYoung-Woo JoKyusang YooYe Lynne KimSang-Hyeon HannYea-Eun KimHyun KimJi-Hoon KimYoung-Yun KongPublished in: Journal of cachexia, sarcopenia and muscle (2024)
has value as a new treatment for SMA that improves treatment effectiveness and reduces adverse events simultaneously.