Real-world outcomes with recombinant factor IX Fc fusion protein (rFIXFc) prophylaxis: Longitudinal follow-up in a national adult cohort.
Mairead O'DonovanCatherine BerginEimear QuinnEvelyn SingletonSheila RocheJulie BensonRachel BirdMary ByrneCleona DugganRuth GilmoreKevin RyanJames S O'DonnellNiamh M O'ConnellPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2021)
This study provides important insights into real-world experience of switching to rFIXFc prophylaxis in an adult population, demonstrating high rates of prophylaxis, with reduced infusion frequency, bleeding and FIX consumption.