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Single cell characterization of B-lymphoid differentiation and leukemic cell states during chemotherapy in ETV6-RUNX1-positive pediatric leukemia identifies drug-targetable transcription factor activities.

Juha MehtonenSusanna TeppoMari LahnalampiAleksi KokkoRiina KaukonenLaura OksaMaria Bouvy-LiivrandAlena MalyukovaArtturi MäkinenSaara LaukkanenPetri I MäkinenSamuli RouniojaPekka RuusuvuoriOlle SangfeltRiikka LundTapio LönnbergOlli LohiMerja Heinäniemi
Published in: Genome medicine (2020)
Our data provide a detailed picture of the transcription factor activities characterizing both normal B-lineage differentiation and those acquired in leukemic bone marrow and provide a rational basis for new treatment strategies targeting the immune microenvironment and the active regulatory network in leukemia.
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