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The Japan Registry for Adult Subjects of Spinal Muscular Atrophy (jREACT-SMA): Protocol for a Longitudinal Observational Study.

Kentaro SahashiAtsushi HashizumeYachiyo KuwatsukaMadoka ChinenAi Saotome-NakamuraMasahiko AndoMasahisa Katsuno
Published in: JMIR research protocols (2022)
DERR1-10.2196/38878.
Keyphrases
  • randomized controlled trial
  • young adults