Longitudinal timed function tests in Duchenne muscular dystrophy: ImagingDMD cohort natural history.
Harneet AroraRebecca J WillcocksDonovan J LottAnn T HarringtonClaudia R SenesacKirsten L ZilkeMichael J DanielsDandan XuGihan I TennekoonErika L FinangerBarry S RussmanRichard S FinkelWilliam T TriplettBarry J ByrneGlenn A WalterH Lee SweeneyKrista VandenbornePublished in: Muscle & nerve (2018)
This study provides insight into the contemporary natural history of key functional endpoints in DMD. Muscle Nerve 58: 631-638, 2018.