Base editing-mediated splicing correction therapy for spinal muscular atrophy.
Xiang LinHaizhu ChenYing-Qian LuShunyan HongXinde HuYanxia GaoLu-Lu LaiJin-Jing LiZishuai WangWenqin YingLixiang MaNing WangErwei ZuoHui YangWan-Jin ChenPublished in: Cell research (2020)
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