Safety, Pharmacokinetics, and Pharmacodynamics of Efzimfotase Alfa, a Second-generation Enzyme Replacement Therapy: Phase 1, Dose-escalation Study in Adults with Hypophosphatasia.
Kathryn McCrystal DahirAmy ShannonDerek DunnWalter VoegtliQunming DongJawad HasanRajendra PradhanRyan PeltoWei-Jian PanPublished in: Journal of bone and mineral research : the official journal of the American Society for Bone and Mineral Research (2024)
NCT04980248.