Molecular therapy. Nucleic acids

Keyphrases

Publications

volume 35, number 3, 2024

Chung-Hsiang Yang, Kuan-Yin Shen, Hui-Min Ho, Chiung-Yi Huang, Yu-Jhen Cheng, Chih-Chun Pu, Fang-Feng Chiu, Wan-Chun Huang, Hung-Chun Liao, Hsin-Wei Chen, Ching-Len Liao, Shih-Jen Liu, Ming-Hsi Huang
Boosting DNA vaccine power by lipid nanoparticles surface engineered with amphiphilic bioresorbable copolymer. Molecular therapy. Nucleic acids 35 (3) (2024)
Chung-Hsiang Yang, Kuan-Yin Shen, Hui-Min Ho, Chiung-Yi Huang, Yu-Jhen Cheng, Chih-Chun Pu, Fang-Feng Chiu, Wan-Chun Huang, Hung-Chun Liao, Hsin-Wei Chen, Ching-Len Liao, Shih-Jen Liu, Ming-Hsi Huang
Boosting DNA vaccine power by lipid nanoparticles surface engineered with amphiphilic bioresorbable copolymer. Molecular therapy. Nucleic acids 35 (3) (2024)
Wenying Yan, Wentao Hu, Yidan Song, Xingyi Liu, Ziyun Zhou, Wanshi Li, Zhifei Cao, Weiwei Pei, Guangming Zhou, Guang Hu
Differential network analysis reveals the key role of the ECM-receptor pathway in α -particle-induced malignant transformation. Molecular therapy. Nucleic acids 35 (3) (2024)
Daniel C Nelson, Urmil M Dave, Norberto Gonzalez-Juarbe
Harnessing mRNA to unleash endolysins: A new frontier in antibacterial therapy. Molecular therapy. Nucleic acids 35 (3) (2024)
Kalina Andrysiak, Paweł E Ferdek, Anna M Sanetra, Gabriela Machaj, Luisa Schmidt, Izabela Kraszewska, Katarzyna Sarad, Katarzyna Palus-Chramiec, Olga Lis, Marta Targosz-Korecka, Marcus Krüger, Marian H Lewandowski, Guillem Ylla, Jacek Stępniewski, Józef Dulak
Upregulation of utrophin improves the phenotype of Duchenne muscular dystrophy hiPSC-derived CMs. Molecular therapy. Nucleic acids 35 (3) (2024)
Adnan Asadbeigi, Mohammad Reza Bakhtiarizadeh, Mojtaba Saffari, Mohammad Hossein Modarressi, Naser Sadri, Zahra Ziafati Kafi, Hassan Fazilaty, Arash Ghalyanchilangeroudi, Hossein Esmaeili
Protection of animals against devastating RNA viruses using CRISPR-Cas13s. Molecular therapy. Nucleic acids 35 (3) (2024)
Ting Wang, Tao Yu, Qian Liu, Tzu-Cheng Sung, Akon Higuchi
Lipid nanoparticle technology-mediated therapeutic gene manipulation in the eyes. Molecular therapy. Nucleic acids 35 (3) (2024)
Anna Jonczyk, Marlene Gottschalk, Matthew S J Mangan, Yasmin Majlesain, Manja W Thiem, Lea-Corinna Burbaum, Heike Weighardt, Eicke Latz, Günter Mayer, Irmgard Förster
Topical application of a CCL22-binding aptamer suppresses contact allergy. Molecular therapy. Nucleic acids 35 (3) (2024)
Mitsuo Kato, Maryam Abdollahi, Keiko Omori, Vajir Malek, Linda Lanting, Fouad Kandeel, Jeffrey Rawson, Walter Tsark, Lingxiao Zhang, Mei Wang, Ragadeepthi Tunduguru, Rama Natarajan
Lowering an ER stress-regulated long noncoding RNA protects mice from diabetes and isolated pancreatic islets from cell death. Molecular therapy. Nucleic acids 35 (3) (2024)
Dong Hun Lee, Ki Cheon Kim, Chul Ju Hwang, Kyung Ran Park, Young Suk Jung, Sun Young Kim, Ji Young Kim, Ju Kyung Song, Min Ji Song, Min Ki Choi, Dae Youn Hwang, Sang-Bae Han, Jin Tae Hong
Retraction Notice to: Decreased Lung Tumor Development in SwAPP Mice through the Downregulation of CHI3L1 and STAT 3 Activity via the Upregulation of miRNA342-3p. Molecular therapy. Nucleic acids 35 (3) (2024)
Mathilde Beaufils, Margaux Melka, Julie Brocard, Clement Benoit, Nagi Debbah, Kamel Mamchaoui, Norma B Romero, Anne Frédérique Dalmas-Laurent, Susana Quijano-Roy, Julien Fauré, John Rendu, Isabelle Marty
Functional benefit of CRISPR-Cas9-induced allele deletion for RYR1 dominant mutation. Molecular therapy. Nucleic acids 35 (3) (2024)
Daniel C Nelson, Urmil M Dave, Norberto Gonzalez-Juarbe
Harnessing mRNA to unleash endolysins: A new frontier in antibacterial therapy. Molecular therapy. Nucleic acids 35 (3) (2024)
Melissa M Evans, Shirley Liu, Joshua S Krautner, Caroline G Seguin, Rajan Leung, John A Ronald
Evaluation of DNA minicircles for delivery of adenine and cytosine base editors using activatable gene on "GO" reporter imaging systems. Molecular therapy. Nucleic acids 35 (3) (2024)
Naoki Iwamoto, Yuanjing Liu, Maria Frank-Kamenetsky, Abbie Maguire, Wei Chou Tseng, Kristin Taborn, Nayantara Kothari, Ali Akhtar, Keith Bowman, Juili Dilip Shelke, Anthony Lamattina, Xiao Shelley Hu, Hyun Gyung Jang, Pachamuthu Kandasamy, Fangjun Liu, Ken Longo, Richard Looby, null Meena, Jake Metterville, Qianli Pan, Erin Purcell-Estabrook, Mamoru Shimizu, Priyanka Shiva Prakasha, Stephany Standley, Hansini Upadhyay, Hailin Yang, Yuan Yin, Anderson Zhao, Christopher Francis, Mike Byrne, Elena Dale, Gregory L Verdine, Chandra Vargeese
Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT . Molecular therapy. Nucleic acids 35 (3) (2024)
Wenbing Jiang, Dongchang Xiao, Cheng Wu, Jiaqi Yang, Xinghua Peng, Linfeng Chen, Jiamin Zhang, Gaofeng Zha, Wei Li, Rong Ju, Mengqing Xiang, Zhi Xie
Circular RNA-based therapy provides sustained and robust neuroprotection for retinal ganglion cells. Molecular therapy. Nucleic acids 35 (3) (2024)
Shuang Li, Renzhi Han
Targeting miR-25 to alleviate DMD-related muscle dysfunction. Molecular therapy. Nucleic acids 35 (3) (2024)
Sara Aguti, Shuzhi Cheng, Pierpaolo Ala, Sean Briggs, Francesco Muntoni, Haiyan Zhou
Strategies to improve the design of gapmer antisense oligonucleotide on allele-specific silencing. Molecular therapy. Nucleic acids 35 (3) (2024)
Jasmin Morandell, Alan Monziani, Martina Lazioli, Deborah Donzel, Jessica Döring, Claudio Oss Pegorar, Angela D'Anzi, Miguel Pellegrini, Andrea Mattiello, Dalia Bortolotti, Guendalina Bergonzoni, Takshashila Tripathi, Virginia B Mattis, Marina Kovalenko, Jessica Rosati, Christoph Dieterich, Erik Dassi, Vanessa C Wheeler, Zdenka Ellederová, Jeremy E Wilusz, Gabriella Viero, Marta Biagioli
CircHTT(2,3,4,5,6) - co-evolving with the HTT CAG-repeat tract - modulates Huntington's disease phenotypes. Molecular therapy. Nucleic acids 35 (3) (2024)
Nikki M McCormack, Kelsey A Calabrese, Christina M Sun, Christopher B Tully, Christopher R Heier, Alyson A Fiorillo
Deletion of miR-146a enhances therapeutic protein restoration in model of dystrophin exon skipping. Molecular therapy. Nucleic acids 35 (3) (2024)
Ting Wang, Tao Yu, Qian Liu, Tzu-Cheng Sung, Akon Higuchi
Lipid nanoparticle technology-mediated therapeutic gene manipulation in the eyes. Molecular therapy. Nucleic acids 35 (3) (2024)
Andreia Vilaça, Carlos Jesus, Miguel Lino, Danika Hayman, Costanza Emanueli, Cesare M Terracciano, Hugo Fernandes, Leon J de Windt, Lino Ferreira
Extracellular vesicle transfer of lncRNA H19 splice variants to cardiac cells. Molecular therapy. Nucleic acids 35 (3) (2024)
Jasmin Morandell, Alan Monziani, Martina Lazioli, Deborah Donzel, Jessica Döring, Claudio Oss Pegorar, Angela D'Anzi, Miguel Pellegrini, Andrea Mattiello, Dalia Bortolotti, Guendalina Bergonzoni, Takshashila Tripathi, Virginia B Mattis, Marina Kovalenko, Jessica Rosati, Christoph Dieterich, Erik Dassi, Vanessa C Wheeler, Zdenka Ellederová, Jeremy E Wilusz, Gabriella Viero, Marta Biagioli
CircHTT(2,3,4,5,6) - co-evolving with the HTT CAG-repeat tract - modulates Huntington's disease phenotypes. Molecular therapy. Nucleic acids 35 (3) (2024)
Amela Jusic, Zoi Erpapazoglou, Louise Torp Dalgaard, Päivi Lakkisto, David de Gonzalo-Calvo, Bettina Benczik, Bence Ágg, Péter Ferdinandy, Katarzyna Fiedorowicz, Blanche Schroen, Antigone Lazou, Yvan Devaux, null null, null null
Guidelines for mitochondrial RNA analysis. Molecular therapy. Nucleic acids 35 (3) (2024)
Amela Jusic, Zoi Erpapazoglou, Louise Torp Dalgaard, Päivi Lakkisto, David de Gonzalo-Calvo, Bettina Benczik, Bence Ágg, Péter Ferdinandy, Katarzyna Fiedorowicz, Blanche Schroen, Antigone Lazou, Yvan Devaux, null null, null null
Guidelines for mitochondrial RNA analysis. Molecular therapy. Nucleic acids 35 (3) (2024)
Mathilde Beaufils, Margaux Melka, Julie Brocard, Clement Benoit, Nagi Debbah, Kamel Mamchaoui, Norma B Romero, Anne Frédérique Dalmas-Laurent, Susana Quijano-Roy, Julien Fauré, John Rendu, Isabelle Marty
Functional benefit of CRISPR-Cas9-induced allele deletion for RYR1 dominant mutation. Molecular therapy. Nucleic acids 35 (3) (2024)
Antonietta Tarallo, Giancarlo Parenti, Nicola Brunetti-Pierri
Precision medicine in action for Pompe disease. Molecular therapy. Nucleic acids 35 (3) (2024)
Anna Jonczyk, Marlene Gottschalk, Matthew S J Mangan, Yasmin Majlesain, Manja W Thiem, Lea-Corinna Burbaum, Heike Weighardt, Eicke Latz, Günter Mayer, Irmgard Förster
Topical application of a CCL22-binding aptamer suppresses contact allergy. Molecular therapy. Nucleic acids 35 (3) (2024)
Mitsuo Kato, Maryam Abdollahi, Keiko Omori, Vajir Malek, Linda Lanting, Fouad Kandeel, Jeffrey Rawson, Walter Tsark, Lingxiao Zhang, Mei Wang, Ragadeepthi Tunduguru, Rama Natarajan
Lowering an ER stress-regulated long noncoding RNA protects mice from diabetes and isolated pancreatic islets from cell death. Molecular therapy. Nucleic acids 35 (3) (2024)
Asger Givskov Jørgensen, Daniel Miotto Dupont, Søren Fjelstrup, Claus Bus, Cecilie Bo Hansen, Thomas Benfield, Peter Garred, Peter M H Heegaard, Jørgen Kjems
Unbiased plasma profiling using pre-selected RNA aptamer pools predicts mortality in COVID-19 and identifies protein risk factors. Molecular therapy. Nucleic acids 35 (3) (2024)
Antonietta Tarallo, Giancarlo Parenti, Nicola Brunetti-Pierri
Precision medicine in action for Pompe disease. Molecular therapy. Nucleic acids 35 (3) (2024)
Bogdan Dume, Emilia Licarete, Manuela Banciu
Advancing cancer treatments: The role of oligonucleotide-based therapies in driving progress. Molecular therapy. Nucleic acids 35 (3) (2024)
Wenbing Jiang, Dongchang Xiao, Cheng Wu, Jiaqi Yang, Xinghua Peng, Linfeng Chen, Jiamin Zhang, Gaofeng Zha, Wei Li, Rong Ju, Mengqing Xiang, Zhi Xie
Circular RNA-based therapy provides sustained and robust neuroprotection for retinal ganglion cells. Molecular therapy. Nucleic acids 35 (3) (2024)
Melissa M Evans, Shirley Liu, Joshua S Krautner, Caroline G Seguin, Rajan Leung, John A Ronald
Evaluation of DNA minicircles for delivery of adenine and cytosine base editors using activatable gene on "GO" reporter imaging systems. Molecular therapy. Nucleic acids 35 (3) (2024)
Bogdan Dume, Emilia Licarete, Manuela Banciu
Advancing cancer treatments: The role of oligonucleotide-based therapies in driving progress. Molecular therapy. Nucleic acids 35 (3) (2024)
Naoki Iwamoto, Yuanjing Liu, Maria Frank-Kamenetsky, Abbie Maguire, Wei Chou Tseng, Kristin Taborn, Nayantara Kothari, Ali Akhtar, Keith Bowman, Juili Dilip Shelke, Anthony Lamattina, Xiao Shelley Hu, Hyun Gyung Jang, Pachamuthu Kandasamy, Fangjun Liu, Ken Longo, Richard Looby, null Meena, Jake Metterville, Qianli Pan, Erin Purcell-Estabrook, Mamoru Shimizu, Priyanka Shiva Prakasha, Stephany Standley, Hansini Upadhyay, Hailin Yang, Yuan Yin, Anderson Zhao, Christopher Francis, Mike Byrne, Elena Dale, Gregory L Verdine, Chandra Vargeese
Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT . Molecular therapy. Nucleic acids 35 (3) (2024)
Kalina Andrysiak, Paweł E Ferdek, Anna M Sanetra, Gabriela Machaj, Luisa Schmidt, Izabela Kraszewska, Katarzyna Sarad, Katarzyna Palus-Chramiec, Olga Lis, Marta Targosz-Korecka, Marcus Krüger, Marian H Lewandowski, Guillem Ylla, Jacek Stępniewski, Józef Dulak
Upregulation of utrophin improves the phenotype of Duchenne muscular dystrophy hiPSC-derived CMs. Molecular therapy. Nucleic acids 35 (3) (2024)
Adnan Asadbeigi, Mohammad Reza Bakhtiarizadeh, Mojtaba Saffari, Mohammad Hossein Modarressi, Naser Sadri, Zahra Ziafati Kafi, Hassan Fazilaty, Arash Ghalyanchilangeroudi, Hossein Esmaeili
Protection of animals against devastating RNA viruses using CRISPR-Cas13s. Molecular therapy. Nucleic acids 35 (3) (2024)
Christophe Delehedde, Ivan Ciganek, Pierre Louis Bernard, Nabila Laroui, Cathy Costa Da Silva, Cristine Gonçalves, Jacques Nunes, Anne-Lise Bennaceur-Griscelli, Jusuf Imeri, Matthias Huyghe, Luc Even, Patrick Midoux, Nathalie Rameix, Geoffrey Guittard, Chantal Pichon
Enhancing natural killer cells proliferation and cytotoxicity using imidazole-based lipid nanoparticles encapsulating interleukin-2 mRNA. Molecular therapy. Nucleic acids 35 (3) (2024)
Shuang Li, Renzhi Han
Targeting miR-25 to alleviate DMD-related muscle dysfunction. Molecular therapy. Nucleic acids 35 (3) (2024)
Sara Aguti, Shuzhi Cheng, Pierpaolo Ala, Sean Briggs, Francesco Muntoni, Haiyan Zhou
Strategies to improve the design of gapmer antisense oligonucleotide on allele-specific silencing. Molecular therapy. Nucleic acids 35 (3) (2024)
Kah Mun Siow, Merve Güngör, Dominik Wrona, Federica Raimondi, Oleksandr Pastukhov, Panagiotis Tsapogas, Timon Menzi, Michael Schmitz, Péter István Kulcsár, Gerald Schwank, Ansgar Schulz, Martin Jinek, Ute Modlich, Ulrich Siler, Janine Reichenbach
Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 phox -deficient chronic granulomatous disease. Molecular therapy. Nucleic acids 35 (3) (2024)
Andreia Vilaça, Carlos Jesus, Miguel Lino, Danika Hayman, Costanza Emanueli, Cesare M Terracciano, Hugo Fernandes, Leon J de Windt, Lino Ferreira
Extracellular vesicle transfer of lncRNA H19 splice variants to cardiac cells. Molecular therapy. Nucleic acids 35 (3) (2024)
Kah Mun Siow, Merve Güngör, Dominik Wrona, Federica Raimondi, Oleksandr Pastukhov, Panagiotis Tsapogas, Timon Menzi, Michael Schmitz, Péter István Kulcsár, Gerald Schwank, Ansgar Schulz, Martin Jinek, Ute Modlich, Ulrich Siler, Janine Reichenbach
Targeted knock-in of NCF1 cDNA into the NCF2 locus leads to myeloid phenotypic correction of p47 phox -deficient chronic granulomatous disease. Molecular therapy. Nucleic acids 35 (3) (2024)
Martina Tuttolomondo, Stephanie Thuy Duong Pham, Mikkel Green Terp, Virginia Cendán Castillo, Nazmie Kalisi, Stefan Vogel, Niels Langkjær, Ulla Melchior Hansen, Helge Thisgaard, Henrik Daa Schrøder, Yaseelan Palarasah, Henrik Jørn Ditzel
A novel multitargeted self-assembling peptide-siRNA complex for simultaneous inhibition of SARS-CoV-2-host cell interaction and replication. Molecular therapy. Nucleic acids 35 (3) (2024)

volume 35, number 4, 2024

Tao Lv, Yichao Jin, Yifeng Miao, Tianqi Xu, Feng Jia, Haizhong Feng, Xiaohua Zhang
Retraction Notice to: LncRNA PVT1 promotes tumorigenesis of glioblastoma by recruiting COPS5 to deubiquitinate and stabilize TRIM24. Molecular therapy. Nucleic acids 35 (4) (2024)
Xia Wu, Mengxin Chen, Kang Liu, Yixin Wu, Yun Feng, Shiting Fu, Huaimeng Xu, Yongqi Zhao, Feilong Lin, Liang Lin, Shihui Ye, Junqiang Lin, Taiping Xiao, Wenhao Li, Meng Lou, Hongyu Lv, Ye Qiu, Ruifan Yu, Wenyan Chen, Mengyuan Li, Xu Feng, Zhongbing Luo, Lu Guo, Hao Ke, Limin Zhao
Molecular classification of geriatric breast cancer displays distinct senescent subgroups of prognostic significance. Molecular therapy. Nucleic acids 35 (4) (2024)
Kelly J Fagan, Guillem Chillon, Ellie M Carrell, Elisa A Waxman, Beverly L Davidson
Cas9 editing of ATXN1 in a spinocerebellar ataxia type 1 mice and human iPSC-derived neurons. Molecular therapy. Nucleic acids 35 (4) (2024)
Hua Huang, Dong Rui Ma, Derrick Wei Shih Chan, Adeline Seow Fen Ngoh, Dejie Yu, Shi Jun Ng, John Jia En Chua, Eng King Tan, Hui-Lin Chin, Denise Li Meng Goh, Tuck Wah Soong
Targeting heterozygous dominant negative variant of KCNA2 using Gapmer ASO for the treatment of drug-resistant epilepsy. Molecular therapy. Nucleic acids 35 (4) (2024)
Ella Borgenheimer, Cameron Trueblood, Bryan L Nguyen, William R Lagor, Joanna L Jankowsky
Simple improvements in vector design afford substantial gains in AAV delivery of aggregation-slowing Aβ variants. Molecular therapy. Nucleic acids 35 (4) (2024)
Camille Huart, Mayuk Saibal Gupta, Jo A Van Ginderachter
The role of RNA modifications in disease-associated macrophages. Molecular therapy. Nucleic acids 35 (4) (2024)