Maria Candida Vila

ORCID

Publication Activity (10 Years)

Years Active: 2015-2023
Publications (10 Years): 3

Top Venues

Epilepsia

Human gene therapy

Skeletal muscle

Audentes Therapeutics Inc

George Washington University (PHD)

This page only lists publications with an associated author ORCID identifier.

Affiliation History

Audentes Therapeutics Inc Mar 11 2019

United States

Senior Manager :: Medical Affairs

Education History

George Washington University Aug 02 2012 - Aug 31 2016

United States

PHD :: Immunology and Microbiology

Publications

Michael Scott Perry, Ingrid Eileen Scheffer, Joseph Sullivan, Andreas Brunklaus, Susana Boronat, James W Wheless, Linda Laux, Anup D Patel, Colin M Roberts, Dennis Dlugos, Deborah Holder, Kelly G Knupp, Matt Lallas, Steven Phillips, Eric Segal, Patricia Smeyers, Dennis Lal, Elaine C Wirrell, Sameer Zuberi, Tobias Brünger, Mary Wojnaroski, Benit Maru, Penrose O'Donnell, Magda Morton, Emma James, Maria Candida Vila, Norman Huang, Jacqueline S Gofshteyn, Salvador Rico
Severe Communication Delays Are Independent of Seizure Burden and Persist Despite Contemporary Treatments in SCN1A+ Dravet Syndrome: Insights from the ENVISION Natural History Study. Epilepsia (2023)
Annie Tanenhaus, Timothy Stowe, Andrew Young, John McLaughlin, Rangoli Aeran, I Winnie Lin, Jianmin Li, Raghavendra Hosur, Ming Chen, Jennifer Leedy, Tiffany Chou, Sirika Pillay, Maria Candida Vila, Jennifer A Kearney, Martin Moorhead, Archana Belle, Stephanie Tagliatela
Cell-Selective Adeno-Associated Virus-Mediated SCN1A Gene Regulation Therapy Rescues Mortality and Seizure Phenotypes in a Dravet Syndrome Mouse Model and Is Well Tolerated in Nonhuman Primates. Human gene therapy 33 (11-12) (2022)
Maria Candida Vila, Margaret Benny Klimek, James S Novak, Sree Rayavarapu, Kitipong Uaesoontrachoon, Jessica F Boehler, Alyson A Fiorillo, Marshall W Hogarth, Aiping Zhang, Conner Shaughnessy, Heather Gordish-Dressman, Umar Burki, Volker Straub, Qi Long Lu, Terence A Partridge, Kristy J Brown, Yetrib Hathout, John van den Anker, Eric P Hoffman, Kanneboyina Nagaraju
Elusive sources of variability of dystrophin rescue by exon skipping. Skeletal muscle 5 (2015)

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Publication Activity (10 Years)

Top Topics

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Maria Candida Vila