Simona Porcellini

Publication Activity (10 Years)

Years Active: 2023-2024
Publications (10 Years): 7

Top Topics

Induced Pluripotent Stem Cells

Replacement Therapy

Top Venues

Science translational medicine

The EMBO journal

This page only lists publications with an associated author ORCID identifier.

Publications

Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M Holland, Jenna R E Bergerson, Suk See De Ravin, Harry L Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M Crooks, Luigi Daniele Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency. Science translational medicine 16 (733) (2024)
Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M Holland, Jenna R E Bergerson, Suk See De Ravin, Harry L Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M Crooks, Luigi Daniele Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency. Science translational medicine 16 (733) (2024)
Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M Holland, Jenna R E Bergerson, Suk See De Ravin, Harry L Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M Crooks, Luigi Daniele Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency. Science translational medicine 16 (733) (2024)
Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M Holland, Jenna R E Bergerson, Suk See De Ravin, Harry L Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M Crooks, Luigi Daniele Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency. Science translational medicine 16 (733) (2024)
Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M Holland, Jenna R E Bergerson, Suk See De Ravin, Harry L Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M Crooks, Luigi Daniele Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency. Science translational medicine 16 (733) (2024)
Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M Holland, Jenna R E Bergerson, Suk See De Ravin, Harry L Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M Crooks, Luigi Daniele Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency. Science translational medicine 16 (733) (2024)
Daniele Canarutto, Claudia Asperti, Valentina Vavassori, Simona Porcellini, Elisabetta Rovelli, Marianna Paulis, Samuele Ferrari, Angelica Varesi, Martina Fiumara, Aurélien Jacob, Lucia Sergi Sergi, Ilaria Visigalli, Francesca Ferrua, Luis Ignacio González-Granado, Vassilios Lougaris, Andrea Finocchi, Anna Villa, Marina Radrizzani, Luigi Naldini
Unbiased assessment of genome integrity and purging of adverse outcomes at the target locus upon editing of CD4 + T-cells for the treatment of Hyper IgM1. The EMBO journal (2023)